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Wilson disease (also called hepatolenticular degeneration) is a rare, autosomal recessive disorder caused by abnormal copper assemblage in the body...

Blincyto, an innovative therapy for certain types of leukemia, presents significant benefits along with potential risks that necessitate careful consideration....

Retevmo (Selpercatanib) is a game-changing medication in the world of oncology, offering targeted therapy for patients with specific genetic alterations...

In the realm of leukemia treatment, Blincyto emerges as a beacon of hope for both adults and children battling specific...

Introduction: T-cell acute lymphoblastic leukemia (T-ALL) is a specific and aggressive type of blood cancer that falls into a broader...

T-cell acute lymphoblastic leukemia/lymphoma (T-ALL/LBL) is a challenging leukemia form mainly affecting adolescents and young adults. While initial treatments can...

Trientine is primarily used for the treatment of Wilson's disease (WD), a genetic condition/disorder that causes copper accumulation in the body. While...

 Dietary restrictions for phenylalanine and tyrosine are commonly recommended in addition to Nitisinone. Patients with HT-1 benefit from a reduced...

Type 1B Oculocutaneous Albinism (OCA) is a rare genetic disorder that affects individuals' pigmentation, causing pale skin, hair, and eyes....

The FDA-approved drug nitisinone treats hereditary tyrosinemia type 1 (HT-1), a rare genetic condition that alters how the amino acid tyrosine is...